ZOLGENSMA Stories
Treated at ~5½ months old
ZOLGENSMA Stories
See how ZOLGENSMA has helped SMA families
Everyone’s spinal muscular atrophy (SMA) story is unique, but many families have faced the same diagnosis, and it can be comforting to hear their personal stories. Why did so many parents and their doctors choose ZOLGENSMA® (onasemnogene abeparvovec-xioi)? Spend some time with Aniya, Brady, Eli, Evelyn, or one of the other children treated with ZOLGENSMA.
Results and outcomes vary among children based on several factors, including how far their SMA symptoms progressed prior to receiving treatment.
Find a story here
Aniya
“Even with 4 copies, we needed to act.”
SMA Type 3 (4 copies of SMN2 gene)
Quinn
“She needed to get treated immediately.”
SMA Type 2 (3 copies of SMN2 gene)
Maisie
“We still wanted ZOLGENSMA because it’s one-time therapy.”
SMA Type 1 (2 copies of SMN2 gene)
Malachi
“He was just gaining more and more strength.”
SMA Type 1 (2 copies of SMN2 gene)
Olivia
“We celebrate Olivia’s treatment day every year.”
SMA Type 1 (2 copies of SMN2 gene)
Evelyn
“The infusion took about an hour. And in the end, everybody clapped.” SMA Type 1 (2 copies of SMN2 gene)
Stella
“The night before I was a ball of nerves.”
SMA Type 1 (2 copies of SMN2 gene)
Lucy
“A chance to live a life in defiance of her diagnosis.”
SMA diagnosed before symptoms (2 copies of SMN2 gene)
Tenley
“She is truly the epitome of never give up.”
SMA Type 1 (2 copies of SMN2 gene)
Adalyne
“ZOLGENSMA was able to give Addy a second chance.”
SMA Type 1 (2 copies of SMN2 gene)
Brady
“From the day we received the diagnosis, our journey went really fast.” SMA Type 2 (3 copies of SMN2 gene)
Donovan
“We’re actually able to see this treatment working.”
SMA Type 1 (2 copies of SMN2 gene)
Eli
“I knew at that point my wish had been granted.”
SMA Type 1 (2 copies of SMN2 gene)
Louis
“So everything is wow!”
SMA Type 1 (2 copies of SMN2 gene)
Matteo
“I want to cook on the moon.”
SMA Type 1 (2 copies of SMN2 gene)
